Global Gaucher Disease Market 2015-2019

Published: Mar 2015 Pages: 88 SKU: IRTNTR5483

Global Gaucher disease market forecast

Gaucher disease is a rare inherited metabolic disorder caused by the deficiency of the enzyme glucocerebrosidase. This, in turn, causes the accumulation of certain detrimental lipids in the body, especially the glycolipid glucocerebroside. The lipids are accumulated mainly within the macrophages, blood cells, spleen, liver, and bone marrow. Approximately 34 genetic mutations have been identified that leads to Gaucher disease, out of which there are four most prominent mutations that lead to more than half of the Gaucher disease globally. Some people may have no symptoms of this disease, while some experience severe complications. Some of the clinical manifestations of this disease are hepatosplenomegaly, anemia, thrombocytopenia, and skeletal abnormalities. According to the Gaucher disease industry analysis, Technavio's analysts predict this market to grow at a CAGR of 7.60 percent over the period 2014-2019.

Covered in this Report

This report covers the present scenario and the growth prospects of the Global Gaucher Disease market for the period 2015-2019. To calculate the Gaucher disease market size & share, the report considers revenue from the sales of various drugs used in the therapy of Gaucher disease, which includes:

• Enzyme replacement therapy

• Substrate reduction therapy

Based on the type of molecule used for the treatment of Gaucher disease, the market is categorized into two segments:

• Biologics

• Small Molecules

Based on the route of administration adopted for the treatment of Gaucher disease, the market is categorized into two segments:

• Oral

• Parenteral

Based on the dosage forms of the drugs used to treat the disease, the Global Gaucher Disease market is categorized into two segments:

• Solid

• Liquid

Technavio's report, Global Gaucher Disease Market 2015-2019, has been prepared based on an in-depth market analysis with inputs from industry experts. The report covers the Americas, and the EMEA and APAC regions; it also covers the global gaucher disease market landscape and its growth prospects in the coming years. The report also includes a discussion of the key vendors operating in this market.

Key Regions

• Americas

• APAC

• EMEA      

Key Vendors

• Actelion Pharmaceuticals

• Genzyme

• Pfizer

• Shire

Other Prominent Vendors

 • Amicus Therapeutics

• Belrose Pharma

• Bionaturis

• Biosidus

• ISU Abxis

• JCR Pharmaceuticals

• LIXTE Biotechnology

• Neuraltus Pharmaceuticals

• Protalix BioTherapeutics

• Teva Pharmaceuticals

• UCB

• Utrecht Holdings

• Zywie

Market Driver

• Special Provisions for Orphan Drugs

• For a full, detailed list, view our report

Market Challenge

• Limited Patient Population

• For a full, detailed list, view our report

Market Trend

• Regulatory Assistance in Emerging Nations

• For a full, detailed list, view our report

Key Questions Answered in this Report

• What will the market size, market revenues, market shares be of the global gaucher disease market in 2019 and what will the growth rate be?

• What are the key market trends in the global gaucher disease market?

• What is driving this market?

• What are the challenges to the market growth of the global gaucher disease market?

• Who are the key vendors in this market space?

• What are the market opportunities and threats faced by the key vendors?

• What are the strengths and weaknesses of the key vendors?

Technavio also provides customized reports based on the specific requirements of our clients.

 

01. Executive Summary
02. List of Abbreviations
03. Scope of the Report
03.1 Market Overview
03.2 Product Offerings
04. Market Research Methodology
04.1 Market Research Process
04.2 Research Methodology
05. Introduction
06. Disease Overview
06.1 Understanding the Disease
06.1.1 Types of Gaucher Disease
06.1.2 Symptoms
06.1.3 Diagnosis
06.2 Etiology
06.3 Epidemiology
06.4 Clinical Manifestations
06.5 Management
06.5.1 Enzyme Replacement Therapy
06.5.2 Substrate Reduction Therapy
06.6 Economic Burden
07. Pipeline Analysis
08. Market Landscape
08.1 Market Overview
08.2 Market Size and Forecast
08.3 Five Forces Analysis
09. Market Segmentation by Type of Therapy
09.1 Enzyme Replacement Therapy
09.2 Substrate Reduction Therapy
10 Market Segmentation by Type of Molecule
10.1 Biologics
10.2 Small Molecules
11 Market Segmentation by Route of Administration
11.1 Oral
11.2 Parenteral
12 Market Segmentation by Dosage Form
12.1 Solid
12.2 Liquid
13 Geographical Segmentation
14 Buying Criteria
15 Market Growth Drivers
16 Drivers and their Impact
17 Market Challenges
18 Impact of Drivers and Challenges
19 Market Trends
20 Trends and their Impact
21 Vendor Landscape
21.1 Competitive Scenario
21.1.1 Key News
21.1.2 Mergers and Acquisitions
21.2 Market Share Analysis 2014
21.2.1 Genzyme
21.2.2 Shire
21.2.3 Actelion Pharmaceuticals
21.2.4 Pfizer
21.3 Other and Future Prominent Vendors
22 Key Vendor Analysis
22.1 Actelion Pharmaceuticals
22.1.1 Key Facts
22.1.2 Business Overview
22.1.3 Geographical Segmentation 2013
22.1.4 Business Strategy
22.1.5 Recent Developments
22.1.6 SWOT Analysis
22.2 Genzyme
22.2.1 Key Facts
22.2.2 Business Overview
22.2.3 Product Segmentation by Revenue 2013
22.2.4 Product Segmentation by Revenue 2012 and 2013
22.2.5 Geographical Segmentation
22.2.6 Business Strategy
22.2.7 Recent Developments
22.2.8 SWOT Analysis
22.3 Pfizer
22.3.1 Key Facts
22.3.2 Business Overview
22.3.3 Business Segmentation by Revenue 2013
22.3.4 Business Segmentation by Revenue 2012 and 2013
22.3.5 Geographical Segmentation by Revenue
22.3.6 Business Strategy
22.3.7 Key Developments
22.3.8 SWOT Analysis
22.4 Shire
22.4.1 Key Facts
22.4.2 Business Overview
22.4.3 Geographical Segmentation by Revenue 2013
22.4.4 Business Strategy
22.4.5 Recent Developments
22.4.6 SWOT Analysis
23 Other Reports in this Series

Research Framework

Technavio presents a detailed picture of the market by way of study, synthesis, and summation of data from multiple sources. The analysts have presented the various facets of the market with a particular focus on identifying the key industry influencers. The data thus presented is comprehensive, reliable, and the result of extensive research, both primary and secondary.

INFORMATION SOURCES

Primary sources

  • Manufacturers and suppliers
  • Channel partners
  • Industry experts
  • Strategic decision makers

Secondary sources

  • Industry journals and periodicals
  • Government data
  • Financial reports of key industry players
  • Historical data
  • Press releases

DATA ANALYSIS

Data Synthesis

  • Collation of data
  • Estimation of key figures
  • Analysis of derived insights

Data Validation

  • Triangulation with data models
  • Reference against proprietary databases
  • Corroboration with industry experts

REPORT WRITING

Qualitative

  • Market drivers
  • Market challenges
  • Market trends
  • Five forces analysis

Quantitative

  • Market size and forecast
  • Market segmentation
  • Geographical insights
  • Competitive landscape

PURCHASE FULL REPORT OF

market

Key Questions Answered

  • What are the key global market and the regional market share?
  • What are the revenue-generating key market segments?
  • What are the key factors driving and challenging this market’s growth?
  • Who are the key market vendors and their growth strategies?
  • What are the latest trends influencing the growth of this market?
  • What are the variables influencing the market growth in the primary regions?
  • What are the factors influencing the growth of the parent market?

Why should you prefer Technavio's market insights report?

  • Off-the-shelf research reports
  • Reports can be tailored to meet the customer's needs
  • Trusted by more than 100 fortune 500 organizations
  • Information about the market's key drivers, trends, and challenges
  • Parent market analysis
  • Every week, 50,000 people visit our subscription platform
  • Detailed vendors report with competitive landscape
  • Covid-19 impact and recovery analysis
  • Data on revenue-generating market segments
  • Details on the market shares of various regions
  • Five-force market analysis