Global Pompe Disease Treatment Market 2016-2020

Table of Contents

PART 01: Executive summary

• Highlights

PART 02: Scope of the report

• Market overview
• Top-vendor offerings

PART 03: Market research methodology

• Research methodology
• Economic indicators

PART 04: Introduction

• Key market highlights

PART 05: Disease overview

• Understanding the disease
• Symptoms
• Diagnosis
• Etiology and pathogenesis
• Biochemical pathway
• Epidemiology
• Management
• Economic burden

PART 06: Market landscape

• Market overview
• Five forces analysis

PART 07: Market segmentation by type of Pompe disease

PART 08: Geographical segmentation

• Pompe disease treatment market in EMEA
• Pompe disease treatment market in Americas
• Pompe disease treatment market in US
• Pompe disease treatment market in APAC

PART 09: Market drivers

• Special regulatory drug designations for orphan drugs
• Reimbursement policies for treatment
• Designated under ICD-10 code
• Shorter development timelines

PART 10: Impact of drivers

PART 11: Market challenges

• Limited patient population
• Weak pipeline
• Lack of long-term commitment

PART 12: Impact of drivers and challenges

PART 13: Market trends

• Focus on gene therapy
• Emergence of immunotherapy for Pompe disease
• Growing public awareness

PART 14: Vendor landscape

• Competitive scenario
• Other prominent vendors

PART 15: Key vendor analysis

• Amicus Therapeutics
• Audentes Therapeutics
• Sanofi Genzyme

PART 16: Appendix

• List of abbreviations

PART 17: Explore Technavio

Research Framework

Technavio presents a detailed picture of the market by way of study, synthesis, and summation of data from multiple sources. The analysts have presented the various facets of the market with a particular focus on identifying the key industry influencers. The data thus presented is comprehensive, reliable, and the result of extensive research, both primary and secondary.

INFORMATION SOURCES

Primary sources

• Manufacturers and suppliers
• Channel partners
• Industry experts
• Strategic decision makers

Secondary sources

• Industry journals and periodicals
• Government data
• Financial reports of key industry players
• Historical data
• Press releases

DATA ANALYSIS

Data Synthesis

• Collation of data
• Estimation of key figures
• Analysis of derived insights

Data Validation

• Triangulation with data models
• Reference against proprietary databases
• Corroboration with industry experts

REPORT WRITING