Global Gene Therapy for Inherited Genetic Disorders Market 2019-2023
- Published: May 2019
- Pages: 125
- SKU: IRTNTR31303
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The global gene therapy for inherited genetic disorders market size will grow by USD 5.81 billion during 2019-2023. This report provides a detailed analysis of the market by application (eye disorders, hematological disorders, central nervous system disorders, muscular disorders, and others) and geography (Asia, Europe, North America, and ROW). The report analyzes the market’s competitive landscape and offers information on several gene therapy drug manufacturers for inherited genetic disorders including BioMarin Pharmaceutical Inc., bluebird bio Inc., Novartis AG, Orchard Therapeutics Plc, and Spark Therapeutics Inc.
Some of the key findings from our gene therapy for inherited genetic disorders market forecast report are summarized below
See the complete table of contents and list of exhibits, as well as selected illustrations and example pages from this report.
Global gene therapy market for inherited genetic disorders: Industry overview
Gene therapy has the potential to cure inherited diseases that cannot be cured using conventional drugs. It is being increasingly adopted in clinical trials because of its high efficacy and safety towards the treatment of inherited genetic disorders. For instance, LUXTURNA, an AAV-based gene therapy is used for the treatment of biallelic RPE65 mutation associated retinal dystrophy. Similarly, Strimvelis, an ex vivo stem cell gene therapy is indicated as a single treatment for patients with ADA-severe combined immunodeficiency. The high efficacy and safety offered by gene therapy will increase the preference for gene therapy treatments for inherited genetic disorders, subsequently driving gene therapy for inherited genetic disorders market growth during the forecast period.
Additionally, upcoming gene therapy for inherited genetic disorders market trends such as the increase in strategic alliances among vendors will also influence the growth of this global market. Vendors in this market are focusing on entering into partnerships to capitalize on the growing demand for curative gene therapies. Merck KGaA and GenScript Biotech Corp. recently formed an alliance to focus on the manufacturing of plasmid and viral vector in China. Many such alliances among vendors will result in the development of novel gene therapies for patients with inherited genetic disorders. As a result of these factors, the global gene therapy for inherited genetic disorders market size will grow at a CAGR of 189%. However, the market’s momentum will decelerate in the coming years because of the decrease in year-over-year growth.
Top gene therapy companies for inherited genetic disorders covered in this market research report
The global gene therapy for inherited genetic disorders market is highly concentrated. This research report provides a detailed analysis of the market’s competitive landscape and provides information on the products offered by various companies. Key insights provided by this gene therapy for inherited genetic disorders market report will help companies create effective strategies to improve their revenue share.
The report offers a detailed analysis of several leading companies including:
- BioMarin Pharmaceutical Inc.
- bluebird bio Inc.
- Novartis AG
- Orchard Therapeutics Plc
- Spark Therapeutics Inc.
Gene therapy for inherited genetic disorders market segmentation based on application
- Eye disorders
- Hematological disorders
- Central nervous system disorders
- Muscular disorders
- Others
Gene therapy was mainly adopted for the treatment of genetic eye disorders in 2018. With the increasing prevalence of hematological disorders across the world, the adoption of gene therapy will increase in hematological disorders applications and this segment will account for the largest market share by the end of the forecast period.
Gene therapy for inherited genetic disorders market segmentation based on geography
- Asia
- Europe
- North America
- ROW
North America will provide maximum growth opportunities for companies in the gene therapy for inherited genetic disorders market. Vendors in the region are developing drugs for inherited genetic disorders that are in the final stages of clinical trials and are expected to be launched during the forecast period. This coupled with the availability of installment-based reimbursement model will contribute to the growth of gene therapy for inherited genetic disorders market growth in North America.
Key highlights of the global gene therapy for inherited genetic disorders market for the forecast period 2019-2023
- CAGR of the market during the forecast period 2019-2023
- Detailed information on factors that will accelerate the growth of the gene therapy for inherited genetic disorders market during the next five years
- Precise estimation of the global gene therapy for inherited genetic disorders market size and its contribution to the parent market
- Accurate predictions on upcoming trends and changes in consumer behavior
- The growth of the gene therapy for inherited genetic disorders industry across Asia, Europe, North America, and ROW
- A thorough analysis of the market’s competitive landscape and detailed information on several vendors
- Comprehensive details of factors that will challenge the growth of gene therapy companies for inherited genetic disorders
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PART 01: EXECUTIVE SUMMARY
PART 02: SCOPE OF THE REPORT
- 2.1 Preface
- 2.2 Preface
- 2.3 Currency conversion rates for US$
PART 03: MARKET LANDSCAPE
- Market ecosystem
- Market characteristics
- Market segmentation analysis
PART 04: MARKET SIZING
- Market definition
- Market sizing 2018
- Market size and forecast 2018-2023
PART 05: FIVE FORCES ANALYSIS
- Bargaining power of buyers
- Bargaining power of suppliers
- Threat of new entrants
- Threat of substitutes
- Threat of rivalry
- Market condition
PART 06: MARKET SEGMENTATION BY APPLICATION
- Market segmentation by application
- Comparison by application
- Eye disorders - Market size and forecast 2018-2023
- Hematological disorders - Market size and forecast 2018-2023
- Central nervous system disorders - Market size and forecast 2018-2023
- Muscular disorders - Market size and forecast 2018-2023
- Others - Market size and forecast 2018-2023
- Market opportunity by application
PART 07: CUSTOMER LANDSCAPE
PART 08: GEOGRAPHIC SEGMENTATION
- Geographic segmentation
- Geographic comparison
- North America - Market size and forecast 2018-2023
- Europe - Market size and forecast 2018-2023
- Asia - Market size and forecast 2018-2023
- ROW - Market size and forecast 2018-2023
- Key leading countries
- Market opportunity
PART 09: DECISION FRAMEWORK
PART 10: DRIVERS AND CHALLENGES
- Market drivers
- Market challenges
PART 11: MARKET TRENDS
- Market trends
PART 12: VENDOR LANDSCAPE
- Overview
- Landscape disruption
PART 13: VENDOR ANALYSIS
- Vendors covered
- Vendor classification
- Market positioning of vendors
- BioMarin Pharmaceutical Inc.
- bluebird bio Inc.
- Novartis AG
- Orchard Therapeutics Plc
- Spark Therapeutics Inc.
PART 14: APPENDIX
- Research methodology
- List of abbreviations
- Definition of market positioning of vendors
PART 15: EXPLORE TECHNAVIO
Research Framework
Technavio presents a detailed picture of the market by way of study, synthesis, and summation of data from multiple sources. The analysts have presented the various facets of the market with a particular focus on identifying the key industry influencers. The data thus presented is comprehensive, reliable, and the result of extensive research, both primary and secondary.
INFORMATION SOURCES
Primary sources
- Manufacturers and suppliers
- Channel partners
- Industry experts
- Strategic decision makers
Secondary sources
- Industry journals and periodicals
- Government data
- Financial reports of key industry players
- Historical data
- Press releases

DATA ANALYSIS
Data Synthesis
- Collation of data
- Estimation of key figures
- Analysis of derived insights
Data Validation
- Triangulation with data models
- Reference against proprietary databases
- Corroboration with industry experts

REPORT WRITING
Qualitative
- Market drivers
- Market challenges
- Market trends
- Five forces analysis
Quantitative
- Market size and forecast
- Market segmentation
- Geographical insights
- Competitive landscape
Key Questions Answered
- What are the key global market and the regional market share?
- What are the revenue-generating key market segments?
- What are the key factors driving and challenging this market’s growth?
- Who are the key market vendors and their growth strategies?
- What are the latest trends influencing the growth of this market?
- What are the variables influencing the market growth in the primary regions?
- What are the factors influencing the growth of the parent market?
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